The Comet Study is an opportunity for you or your loved one to be part of a study testing a potential new treatment option.
The Comet Study is your chance to have a say in what comes next with Pompe disease. We are looking for patients with untreated late-onset Pompe disease to take part in a clinical research study. The purpose of this study is to compare the safety and effectiveness of two enzyme replacement therapies in patients with late-onset Pompe disease.
Individuals will be evaluated to determine their eligibility to participate in the study. Each patient who qualifies will receive either the study drug or the currently approved therapy, study-related procedures, and laboratory tests at no cost. Reimbursement for time and travel may also be available. Learn more about the Comet Study.
See If You May Qualify
View full list of participating site locations.